1.1 List of Tables
Table 1: Number of Products under Development for Sickle Cell Disease 8
Table 2: Number of Products under Development by Companies, Sickle Cell Disease 9
Table 3: Number of Products under Development by Universities/Institutes, Sickle Cell Disease 11
Table 4: Products under Development by Companies, Sickle Cell Disease 12
Table 5: Products under Development by Universities/Institutes, Sickle Cell Disease 14
Table 6: Number of Products under Development for Vaso-Occlusive Crisis Associated With Sickle Cell Disease 15
Table 7: Number of Products under Development by Companies, Vaso-Occlusive Crisis Associated With Sickle Cell Disease 16
Table 8: Products under Development by Companies, Vaso-Occlusive Crisis Associated With Sickle Cell Disease 17
Table 9: Number of Products by Stage and Target, Sickle Cell Disease 19
Table 10: Number of Products by Stage and Mechanism of Action, Sickle Cell Disease 21
Table 11: Number of Products by Stage and Route of Administration, Sickle Cell Disease 23
Table 12: Number of Products by Stage and Molecule Type, Sickle Cell Disease 24
Table 13: Number of Products by Stage and Target, Vaso-Occlusive Crisis Associated With Sickle Cell Disease 26
Table 14: Number of Products by Stage and Mechanism of Action, Vaso-Occlusive Crisis Associated With Sickle Cell Disease 27
Table 15: Number of Products by Stage and Route of Administration, Vaso-Occlusive Crisis Associated With Sickle Cell Disease 29
Table 16: Number of Products by Stage and Molecule Type, Vaso-Occlusive Crisis Associated With Sickle Cell Disease 30
Table 17: Sickle Cell Disease – Pipeline by Acceleron Pharma Inc 31
Table 18: Sickle Cell Disease – Pipeline by Addmedica SAS 31
Table 19: Sickle Cell Disease – Pipeline by Angiocrine Bioscience Inc 32
Table 20: Sickle Cell Disease – Pipeline by Annexin Pharmaceuticals AB 32
Table 21: Sickle Cell Disease – Pipeline by ArQule Inc 33
Table 22: Sickle Cell Disease – Pipeline by Bio Products Laboratory Ltd 33
Table 23: Sickle Cell Disease – Pipeline by Bioverativ Inc 34
Table 24: Sickle Cell Disease – Pipeline by bluebird bio Inc 35
Table 25: Sickle Cell Disease – Pipeline by Bristol-Myers Squibb Co 35
Table 26: Sickle Cell Disease – Pipeline by Calimmune Inc 36
Table 27: Sickle Cell Disease – Pipeline by CRISPR Therapeutics 36
Table 28: Sickle Cell Disease – Pipeline by CSL Ltd 37
Table 29: Sickle Cell Disease – Pipeline by Daiichi Sankyo Co Ltd 37
Table 30: Sickle Cell Disease – Pipeline by Editas Medicine Inc 38
Table 31: Sickle Cell Disease – Pipeline by Errant Gene Therapeutics LLC 38
Table 32: Sickle Cell Disease – Pipeline by Gamida Cell Ltd 38
Table 33: Sickle Cell Disease – Pipeline by Genethon SA 39
Table 34: Sickle Cell Disease – Pipeline by Gilead Sciences Inc 39
Table 35: Sickle Cell Disease – Pipeline by Global Blood Therapeutics Inc 40
Table 36: Sickle Cell Disease – Pipeline by Incyte Corp 40
Table 37: Sickle Cell Disease – Pipeline by Ironwood Pharmaceuticals Inc 41
Table 38: Sickle Cell Disease – Pipeline by La Jolla Pharmaceutical Company 41
Table 39: Sickle Cell Disease – Pipeline by MaxCyte Inc 42
Table 40: Sickle Cell Disease – Pipeline by Merck & Co Inc 43
Table 41: Sickle Cell Disease – Pipeline by Morphogenesis Inc 43
Table 42: Sickle Cell Disease – Pipeline by NKT Therapeutics Inc 43
Table 43: Sickle Cell Disease – Pipeline by Novartis AG 44
Table 44: Sickle Cell Disease – Pipeline by Orphagen Pharmaceuticals Inc 44
Table 45: Sickle Cell Disease – Pipeline by Prolong Pharmaceuticals LLC 45
Table 46: Sickle Cell Disease – Pipeline by Protagonist Therapeutics Inc 45
Table 47: Sickle Cell Disease – Pipeline by ReveraGen BioPharma Inc 46
Table 48: Sickle Cell Disease – Pipeline by Sancilio & Company Inc 46
Table 49: Sickle Cell Disease – Pipeline by Sangamo Therapeutics Inc 46
Table 50: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by AstraZeneca Plc 47
Table 51: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Bristol-Myers Squibb Co 48
Table 52: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Gilead Sciences Inc 48
Table 53: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Modus Therapeutics Holding AB 49
Table 54: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Novartis AG 49
Table 55: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by NuvOx Pharma LLC 50
Table 56: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Pfizer Inc 50
Table 57: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Prolong Pharmaceuticals LLC 51
Table 58: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Pipeline by Seattle Genetics Inc 51
Table 59: Sickle Cell Disease – Dormant Projects 52
Table 60: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Dormant Projects 54
Table 61: Vaso-Occlusive Crisis Associated With Sickle Cell Disease – Discontinued Products 55